Clinical trials · Pennsylvania
Friedreich Ataxia clinical trials in Pennsylvania
We’re tracking 6 recruiting friedreich ataxia studies with a site in Pennsylvania — including Phase 1, Phase 2 and Phase 3 studies, each written for real people, not researchers.
Recruiting studies in Pennsylvania
- NCT06016946Recruiting
Friedreich's Ataxia Natural History Study
This study follows people with Friedreich's ataxia (FA) over time to learn more about the disease. It helps researchers understand how FA affects people of all ages and may lead to better treatments.
Philadelphia, PennsylvaniaAges Any age - NCT06447025RecruitingPhase 2
Study of CTI-1601 for people with Friedreich's ataxia
This trial tests an injectable medicine called CTI-1601 for Friedreich's ataxia (FRDA). It is an open-label study, meaning everyone knows they are getting the drug. The study is for people who have taken CTI-1601 before (without serious side effects) or are new to the drug.
Philadelphia, PennsylvaniaAges 2–60 - NCT06953583RecruitingPhase 3
Testing omaveloxolone for children and teens with Friedreich's Ataxia
This study tests a drug called omaveloxolone (BIIB141) for children and teens with Friedreich’s Ataxia. It looks at how well the drug works and how safe it is over a longer time.
Philadelphia, PennsylvaniaAges 2–15 - NCT07180355RecruitingPhase 1
Gene therapy trial for Friedreich's ataxia
This trial tests a gene therapy called SGT-212 for people with Friedreich's ataxia. It aims to help treat the condition by delivering a working copy of the gene.
Philadelphia, PennsylvaniaAges 18–40 - NCT06623890Recruiting
Long-term safety of omaveloxolone for Friedreich's ataxia
This study looks at the long-term safety of omaveloxolone (BIIB141) for people with Friedreich's ataxia. You can join if you are just starting this medicine or have been taking it for less than a year.
Philadelphia, PennsylvaniaAges 16 years+ - NCT07635030Enrolling by invitation
Brain Chemistry Study in Young People with Friedreich's Ataxia
This study looks at two brain chemicals (GABA and glutathione) in children and teens aged 8–15 with Friedreich's ataxia, a rare genetic condition affecting movement and coordination. The research aims to understand how these chemicals change in the brain and may help guide future treatments.
Philadelphia, PennsylvaniaAges 8–16
Friedreich Ataxia trials by city in Pennsylvania
Where these studies are running in Pennsylvania
Institutions with a site for the recruiting friedreich ataxia studies listed above.
- Children's Hospital of Philadelphia · 6 studies
What taking part in a friedreich ataxia study involves
A screening visit first
Before anything else, the study team checks whether you fit — usually a visit with some tests. You can stop at any point, and screening is typically free.
Care at a nearby site
Study visits happen at a clinic or hospital taking part. Many studies cover the cost of the study treatment and related visits, and some reimburse travel.
You stay in control
Taking part is voluntary and you can leave a study at any time, for any reason, without affecting your regular care.
The team decides eligibility
Our fit check is a helpful first read, not a decision. The study team makes the final call after reviewing your health history.
Friedreich Ataxia trials in other states
Common questions
- Are there friedreich ataxia clinical trials in Pennsylvania?
- Yes. We're currently tracking 6 recruiting friedreich ataxia studies with a site in Pennsylvania, each rewritten in plain language so you can see what it's testing and who it's for.
- How do I find out if I qualify for a friedreich ataxia study in Pennsylvania?
- Each study lists its eligibility rules — age, diagnosis, prior treatments. On every trial page we explain these in plain language and offer a short, optional pre-screen for a fit read. The study team makes the final decision.
- Do I have to live in Pennsylvania to take part?
- Not necessarily. These studies have a site in Pennsylvania, but eligibility is about your health, not your address — some people travel to take part, and a few studies reimburse travel. The study team can tell you what's required.
- Does it cost anything to join a friedreich ataxia trial?
- Using Clin2 is always free. Many trials cover the study treatment and related visits; some reimburse travel. The study team explains exactly what's covered before you decide.
Not the right time?
New friedreich ataxia studies open in Pennsylvania regularly. Set up a health profile and we’ll quietly watch for studies that fit you and email you when one opens.
Clin2 helps you find and understand clinical trials and does not provide medical advice. Study data comes from ClinicalTrials.gov. Talk with your doctor about whether a specific trial is right for you.