Clinical trials · North Carolina
Gaucher Disease clinical trials in North Carolina
We’re tracking 4 recruiting gaucher disease studies with a site in North Carolina — including Phase 1/Phase 2 and Phase 3 studies, each written for real people, not researchers.
Recruiting studies in North Carolina
- NCT03190837Recruiting
Long-term study for people with Gaucher disease
This study is designed to learn what happens over time in people who have Gaucher disease. It may help researchers understand the long-term effects of the condition and improve future care.
Durham, North CarolinaAges Any age - NCT05487599RecruitingPhase 1/Phase 2
Tested new drug for Gaucher disease affecting blood and bones
This early-phase study tests PR001 in adults with Gaucher disease that affects organs and symptoms in the body. If you’re already on enzyme treatment, the trial checks whether this new treatment can safely help you, while doctors closely monitor side effects and organ changes.
Durham, North CarolinaAges 18 years+ - NCT00358943Recruiting
Gaucher disease registry and pregnancy tracking study
This study creates a large, long-term record of people with Gaucher disease and details about pregnancy outcomes. It helps researchers better understand Gaucher over a person’s life and during pregnancy.
Durham, North CarolinaAges Any age - NCT07223944RecruitingPhase 3
Gene therapy trial for Gaucher disease type 1
This trial tests a gene therapy called FLT201 for adults with Gaucher disease type 1. It aims to provide a long-term treatment option for people who have been stable on enzyme replacement therapy (ERT) or substrate reduction therapy (SRT) for at least two years.
Durham, North CarolinaAges 18 years+
Gaucher Disease trials by city in North Carolina
Where these studies are running in North Carolina
Institutions with a site for the recruiting gaucher disease studies listed above.
- Duke University Medical Center · 3 studies
- Carolinas Medical Center/Levine Cancer Institute
- Duke University Health System
What taking part in a gaucher disease study involves
A screening visit first
Before anything else, the study team checks whether you fit — usually a visit with some tests. You can stop at any point, and screening is typically free.
Care at a nearby site
Study visits happen at a clinic or hospital taking part. Many studies cover the cost of the study treatment and related visits, and some reimburse travel.
You stay in control
Taking part is voluntary and you can leave a study at any time, for any reason, without affecting your regular care.
The team decides eligibility
Our fit check is a helpful first read, not a decision. The study team makes the final call after reviewing your health history.
Gaucher Disease trials in other states
Common questions
- Are there gaucher disease clinical trials in North Carolina?
- Yes. We're currently tracking 4 recruiting gaucher disease studies with a site in North Carolina, each rewritten in plain language so you can see what it's testing and who it's for.
- How do I find out if I qualify for a gaucher disease study in North Carolina?
- Each study lists its eligibility rules — age, diagnosis, prior treatments. On every trial page we explain these in plain language and offer a short, optional pre-screen for a fit read. The study team makes the final decision.
- Do I have to live in North Carolina to take part?
- Not necessarily. These studies have a site in North Carolina, but eligibility is about your health, not your address — some people travel to take part, and a few studies reimburse travel. The study team can tell you what's required.
- Does it cost anything to join a gaucher disease trial?
- Using Clin2 is always free. Many trials cover the study treatment and related visits; some reimburse travel. The study team explains exactly what's covered before you decide.
Not the right time?
New gaucher disease studies open in North Carolina regularly. Set up a health profile and we’ll quietly watch for studies that fit you and email you when one opens.
Clin2 helps you find and understand clinical trials and does not provide medical advice. Study data comes from ClinicalTrials.gov. Talk with your doctor about whether a specific trial is right for you.