Clin2
NCT00358943Likely a fitRecruiting

Gaucher disease registry and pregnancy tracking study

Gaucher DiseaseCerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency DiseaseGlucosylceramide Beta-Glucosidase Deficiency Disease

Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.

This study creates a large, long-term record of people with Gaucher disease and details about pregnancy outcomes. It helps researchers better understand Gaucher over a person’s life and during pregnancy.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
12,000 people
Ages
Any age
Study type
Observational

Who can take part

  • You have a confirmed diagnosis of Gaucher disease
  • Your diagnosis must be documented by enzyme testing and/or a gene change
  • You must agree to be included and sign the permission forms
  • If joining the pregnancy part, you must be pregnant or have been pregnant before
  • You must have pregnancy information documented by your medical team

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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