Clinical trials · Washington, D.C., DC
Gaucher Disease clinical trials in Washington, D.C.
We’re tracking 4 recruiting gaucher disease studies with a site in or near Washington, D.C. — including Phase 1/Phase 2 and Phase 3 studies, each written for real people, not researchers.
Recruiting studies near Washington, D.C.
- NCT00358943Recruiting
Gaucher disease registry and pregnancy tracking study
This study creates a large, long-term record of people with Gaucher disease and details about pregnancy outcomes. It helps researchers better understand Gaucher over a person’s life and during pregnancy.
Washington D.C., District of ColumbiaAges Any age - NCT00001215Enrolling by invitation
Understanding Genetic Lysosomal Storage Disorders
This study aims to understand genetic factors in lysosomal storage disorders—rare conditions where the body cannot break down certain substances. Researchers will collect information from patients with these disorders, their family members, and healthy volunteers to learn how these diseases develop and affect people over time.
Bethesda, MarylandAges 1 week–110 years - NCT07223944RecruitingPhase 3
Gene therapy trial for Gaucher disease type 1
This trial tests a gene therapy called FLT201 for adults with Gaucher disease type 1. It aims to provide a long-term treatment option for people who have been stable on enzyme replacement therapy (ERT) or substrate reduction therapy (SRT) for at least two years.
Fairfax, VirginiaAges 18 years+ - NCT05487599RecruitingPhase 1/Phase 2
Tested new drug for Gaucher disease affecting blood and bones
This early-phase study tests PR001 in adults with Gaucher disease that affects organs and symptoms in the body. If you’re already on enzyme treatment, the trial checks whether this new treatment can safely help you, while doctors closely monitor side effects and organ changes.
Fairfax, VirginiaAges 18 years+
Hear when a new Gaucher Disease trial opens near Washington, D.C., DC
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Gaucher Disease trials in other cities
Where these studies are running near Washington, D.C.
Institutions with a site for the recruiting gaucher disease studies listed above.
- Lysosomal and Rare Disorders Research and Treatment Center · 2 studies
- Children's National Medical Center
- Johns Hopkins University
- National Institutes of Health Clinical Center
- O & O Alpan
- Site Number - 1024, 1040, 250012
What taking part in a gaucher disease study involves
A screening visit first
Before anything else, the study team checks whether you fit — usually a visit with some tests. You can stop at any point, and screening is typically free.
Care at a nearby site
Study visits happen at a clinic or hospital taking part. Many studies cover the cost of the study treatment and related visits, and some reimburse travel.
You stay in control
Taking part is voluntary and you can leave a study at any time, for any reason, without affecting your regular care.
The team decides eligibility
Our fit check is a helpful first read, not a decision. The study team makes the final call after reviewing your health history.
Common questions
- Are there gaucher disease clinical trials near Washington, D.C.?
- Yes. We're currently tracking 4 recruiting gaucher disease studies with a site near Washington, D.C., each rewritten in plain language so you can see what it's testing and who it's for.
- How do I find out if I qualify for a gaucher disease study near Washington, D.C.?
- Each study lists its eligibility rules — age, diagnosis, prior treatments. On every trial page we explain these in plain language and offer a short, optional pre-screen for a fit read. The study team makes the final decision.
- Do I have to live in Washington, D.C. to take part?
- Not necessarily. These studies have a site near Washington, D.C., but eligibility is about your health, not your address — some people travel to take part, and a few studies reimburse travel. The study team can tell you what's required.
- Does it cost anything to join a gaucher disease trial?
- Using Clin2 is always free. Many trials cover the study treatment and related visits; some reimburse travel. The study team explains exactly what's covered before you decide.
Not the right time?
New gaucher disease studies open near Washington, D.C. regularly. Set up a health profile and we’ll quietly watch for studies that fit you and email you when one opens.