Clin2
NCT04101968Possibly a fitRecruiting

Study of GBA changes in Parkinson’s using multiple tests

Parkinson DiseaseGBA Gene MutationGaucher Disease

Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.

This study looks at people with Parkinson’s who carry a specific genetic change in the GBA gene. It uses several tests (including brain scans) to understand the disease better and may help guide future treatments.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
25 people
Ages
18 years to 80 years
Study type
Observational

Who can take part

  • You’re between 18 and 80 years old.
  • Your genetic test shows a harmful (pathogenic) GBA change, or a known GBA variant.
  • You do not have another neurological disorder along with Parkinson’s.
  • You can safely have MRI brain scans (no incompatible implants or metal devices).
  • You do not have severe claustrophobia (strong fear of being in a small space).
  • You can tolerate stopping certain Parkinson’s medicines if you are asked to (if you have GBA-PD).

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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