Clin2
NCT04208529Likely a fitEnrolling by invitation

Long-term follow-up after receiving CTX001 infusion

Beta-ThalassemiaThalassemiaSickle Cell DiseaseHematologic DiseasesHemoglobinopathiesGenetic Diseases, InbornSickle Cell Anemia

Part of Blood & lymphatic, Genetic & congenital clinical trials.

This study follows people for a long time after they received CTX001 in an earlier (parent) study. It helps researchers learn about long-term safety and outcomes of the treatment.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 3
Enrollment
160 people
Ages
2 years and older
Study type
Interventional

Who can take part

  • You must sign and date the informed consent form (and assent if it applies).
  • If you cannot consent, your legal guardian or authorized representative must consent for you.
  • You must have received a CTX001 infusion in the earlier parent study.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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