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NCT05667493Possibly a fitEnrolling by invitation

Long-term safety follow-up for eplontersen in ATTR heart disease

Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)

Part of Hormones & metabolism clinical trials.

This is a long-term study to check the safety of eplontersen over time in adults with transthyretin-mediated amyloid cardiomyopathy (ATTR-CM). It is mainly for people who already took the study medication before, or who joined an earlier related study and are doing well.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 3
Enrollment
1,400 people
Ages
18 years and older
Study type
Interventional

Who can take part

  • You finished the earlier main study (or were in a related earlier study for ATTR-CM) and did well in it
  • Your doctor is willing to restart you on eplontersen in an open-label (no-unknowns) way
  • You can take vitamin A as instructed in the study plan
  • You did not permanently stop the study drug during the earlier main/related studies
  • No new health problem or worsening condition is making you unsuitable or interfering with the study

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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