Clin2
NCT06103487Likely a fitEnrolling by invitation

Long-term follow-up for RGX-111 treatment

Mucopolysaccharidosis I

Part of Genetic & congenital, Hormones & metabolism, Skin clinical trials.

This study follows participants who previously received the RGX-111 treatment to monitor their health over time. It helps researchers understand the long-term effects and safety of the therapy.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
21 people
Ages
Any age
Study type
Observational

Who can take part

  • You must have received RGX-111 in a previous study.
  • You or your legal guardian must agree to participate and sign a consent form.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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