Gene therapy for severe hemophilia A
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This trial tests a gene therapy to help your body produce more of the clotting protein (factor VIII) it's missing. It may reduce or stop the need for regular factor infusions.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are a man aged 18 or older.
- You have severe hemophilia A.
- You have had factor VIII treatment at least 150 times before.
- You have never had a severe allergic reaction to factor VIII.
- You are willing to use birth control during the study.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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