Gene therapy safety study for severe hemophilia B
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This study tests a new gene therapy called ANB-002 for men with severe hemophilia B (factor IX levels at or below 2%). The goal is to see if it's safe and how well it might help your blood clot normally.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be a man with hemophilia B.
- You must be at least 18 years old.
- Your factor IX activity must be 2% or less (severe hemophilia B) and you must not have inhibitors.
- You must have had at least 150 days of treatment with factor IX concentrates in the past.
- You cannot have received gene therapy before.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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