CS-101 for patients with beta-thalassemia
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This trial tests a new treatment called CS-101 for people with beta-thalassemia who need regular blood transfusions. It aims to see if CS-101 can help reduce transfusion needs.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be between 6 and 35 years old.
- You have been diagnosed with beta-thalassemia.
- You have needed at least 8 blood transfusions in the past year.
- You are generally healthy enough for the study procedures.
- You have not had a stem cell transplant or gene therapy before.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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