Diet and Cysteine for Children with Homocystinuria
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism, Skin clinical trials.
This trial tests whether adding a special diet and cysteine supplements can help children with a specific type of homocystinuria grow better and control their lab results. It is for Qatari children who are already following a diet for this condition.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have a confirmed diagnosis of classic homocystinuria (HCU) that does not respond to vitamin B6.
- You were diagnosed through newborn screening or by a specialist.
- You are currently following a special diet for homocystinuria.
- You are between birth and 18 years old.
- You are willing to take part in the study.
- You are a Qatari patient.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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