Clin2
NCT07633951Likely a fitNot yet recruiting

Antibody Study for Gene Therapy in Muscle Diseases

Neuromuscular DeficitsGenetic Disorder

Part of Genetic & congenital clinical trials.

This study measures your body's natural immune response to certain viruses used in experimental gene therapies for inherited muscle diseases. Results help doctors understand who might be a good candidate for these treatments in the future.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
450 people
Ages
6 years to 60 years
Study type
Interventional

Who can take part

  • You are between 6 and 59 years old
  • You have been diagnosed with an inherited muscle or nerve disease
  • You have not received any gene therapy or cell therapy treatments before
  • You have signed an informed consent form agreeing to participate
  • You have health insurance coverage
  • For patients under 18, parents or guardians must agree you can participate

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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