Study of Zolgensma for spinal muscular atrophy
Part of Brain & nervous system clinical trials.
This study looks at how safe and effective Zolgensma is when given as an injection into the spinal fluid. It's for people with spinal muscular atrophy who have already been treated with Zolgensma.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have been treated with Zolgensma for spinal muscular atrophy.
- You have not received Zolgensma for unapproved uses outside of this study's guidelines.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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