Clin2
NCT07796022Possibly a fitNot yet recruiting

Thalassemia burden study for children and teens

Thalassemia Particularly Transfusion Dependent Thalassemia

Part of Blood & lymphatic, Genetic & congenital clinical trials.

This study looks at the physical, emotional, and financial challenges faced by children and teens with thalassemia in Sohag, Egypt. Participation involves regular follow-up at a specific clinic and answering questions about your experiences, which may help improve care.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
100 people
Ages
2 years to 18 years
Study type
Observational

Who can take part

  • You are between 2 and 18 years old
  • You have been diagnosed with thalassemia
  • You get regular care at a participating pediatric hematology clinic or thalassemia unit in Sohag
  • You do not have other blood disorders unrelated to thalassemia
  • You are not seriously ill at the time of the study
  • You and your caregiver agree to take part

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

Similar studies

Other trials that look related to this one.

NCT06720480Not yet recruiting
Thalassemia severity study for children and teens

This study looks at how severe thalassemia is in children and teens. It may help doctors understand the condition better and improve care.

NCT07288762Not yet recruiting
Checking reproductive health in teens with thalassemia

This study looks at how blood transfusions for thalassemia may affect the reproductive system (gonads) in teenagers. It aims to find out if there are any issues so they can be managed early.

NCT07204015Not yet recruiting
Body composition in children with thalassemia major

This study looks at how blood transfusions and thalassemia affect body composition (like muscle and fat) in children. It may help doctors understand and manage growth and nutrition better.

NCT06465550Recruiting· Phase 1
Gene therapy for beta-thalassemia in children and teens

This trial tests a new gene therapy (BD211) for children and teens with severe beta-thalassemia who need regular blood transfusions. The treatment uses your own blood stem cells, modified with a working gene, to help your body make healthy red blood cells and reduce the need for transfusions.

Guangzhou, Guandong
NCT04143724Recruiting· Phase 2
Luspatercept for children with beta-thalassemia

This study tests a medicine called luspatercept to see if it safely helps children with beta-thalassemia need fewer blood transfusions or keep their hemoglobin levels stable. It is for children aged 6 to 17 who either get regular transfusions or have low hemoglobin and few transfusions.

Los Angeles, California
NCT07055503Enrolling by invitation
Testing a new blood storage system for thalassemia transfusions

This study tests a special system (Hemanext One) that stores red blood cells with less oxygen, to see if it helps people with thalassemia who need regular transfusions. It may reduce side effects or improve how well the transfusions work.

Athens, Attica

Hear when a new Thalassemia Particularly Transfusion Dependent Thalassemia trial opens

We’ll email you when one opens — at most once a week, no account needed, unsubscribe anytime.