Are there neurofibromatosis 1 clinical trials in Pennsylvania?

Yes. We're currently tracking 4 recruiting neurofibromatosis 1 studies with a site in Pennsylvania, each rewritten in plain language so you can see what it's testing and who it's for.

How do I find out if I qualify for a neurofibromatosis 1 study in Pennsylvania?

Each study lists its eligibility rules — age, diagnosis, prior treatments. On every trial page we explain these in plain language and offer a short, optional pre-screen for a fit read. The study team makes the final decision.

Do I have to live in Pennsylvania to take part?

Not necessarily. These studies have a site in Pennsylvania, but eligibility is about your health, not your address — some people travel to take part, and a few studies reimburse travel. The study team can tell you what's required.

Does it cost anything to join a neurofibromatosis 1 trial?

Using Clin2 is always free. Many trials cover the study treatment and related visits; some reimburse travel. The study team explains exactly what's covered before you decide.

Clinical trials · Pennsylvania

Neurofibromatosis 1 clinical trials in Pennsylvania

We’re tracking 4 recruiting neurofibromatosis 1 studies with a site in Pennsylvania — including Phase 1/Phase 2 and Phase 2 studies, each written for real people, not researchers.

Recruiting studies in Pennsylvania

NCT06541847RecruitingPhase 2
Testing HLX-1502 for NF1 with Plexiform Neurofibromas
This trial tests an experimental drug called HLX-1502 for people with NF1 who have a plexiform neurofibroma (a type of nerve tumor) that is growing or causing problems. It aims to see if the drug is safe and can shrink or stop the tumor from worsening.
Philadelphia, PennsylvaniaAges 12 years+
NCT02544022Recruiting
Testing and validating pain and symptom questionnaires for NF1
This study checks whether patient surveys (questionnaires) can reliably measure symptoms and pain in people with NF1 who have plexiform neurofibromas. It helps create better tools for tracking how you feel and how treatments may affect quality of life.
Philadelphia, PennsylvaniaAges 5 years+
NCT06188741RecruitingPhase 2
Selumetinib to prevent tumor growth in NF1 children
This study tests whether the drug selumetinib can prevent the growth of plexiform neurofibromas (nerve tumors) in young children with NF1. Children are first monitored with MRI scans, and if a tumor appears or grows, they may receive treatment.
Philadelphia, PennsylvaniaAges 1–8
NCT05849662RecruitingPhase 1/Phase 2
Trametinib plus azacitidine for newly diagnosed JMML
This trial studies whether trametinib and azacitidine can control juvenile myelomonocytic leukemia (JMML) soon after diagnosis. It’s designed to test safety and how well the treatment works in children and young adults who meet specific leukemia and genetic criteria.
Philadelphia, PennsylvaniaAges 1 month–21 years

Neurofibromatosis 1 trials by city in Pennsylvania

Philadelphia

Where these studies are running in Pennsylvania

Institutions with a site for the recruiting neurofibromatosis 1 studies listed above.

Children's Hospital of Philadelphia · 4 studies

What taking part in a neurofibromatosis 1 study involves

A screening visit first

Before anything else, the study team checks whether you fit — usually a visit with some tests. You can stop at any point, and screening is typically free.

Care at a nearby site

Study visits happen at a clinic or hospital taking part. Many studies cover the cost of the study treatment and related visits, and some reimburse travel.

You stay in control

Taking part is voluntary and you can leave a study at any time, for any reason, without affecting your regular care.

The team decides eligibility

Our fit check is a helpful first read, not a decision. The study team makes the final call after reviewing your health history.

Neurofibromatosis 1 trials in other states

Common questions

Are there neurofibromatosis 1 clinical trials in Pennsylvania?: Yes. We're currently tracking 4 recruiting neurofibromatosis 1 studies with a site in Pennsylvania, each rewritten in plain language so you can see what it's testing and who it's for.
How do I find out if I qualify for a neurofibromatosis 1 study in Pennsylvania?: Each study lists its eligibility rules — age, diagnosis, prior treatments. On every trial page we explain these in plain language and offer a short, optional pre-screen for a fit read. The study team makes the final decision.
Do I have to live in Pennsylvania to take part?: Not necessarily. These studies have a site in Pennsylvania, but eligibility is about your health, not your address — some people travel to take part, and a few studies reimburse travel. The study team can tell you what's required.
Does it cost anything to join a neurofibromatosis 1 trial?: Using Clin2 is always free. Many trials cover the study treatment and related visits; some reimburse travel. The study team explains exactly what's covered before you decide.

Not the right time?

New neurofibromatosis 1 studies open in Pennsylvania regularly. Set up a health profile and we’ll quietly watch for studies that fit you and email you when one opens.

Get told when a study that fits you opens

Clin2 helps you find and understand clinical trials and does not provide medical advice. Study data comes from ClinicalTrials.gov. Talk with your doctor about whether a specific trial is right for you.