Clin2
NCT03581240Possibly a fitAvailable

DFMO for rare childhood cancers

NeuroblastomaMedulloblastomaTypical Teratoid Rhabdoid TumorEmbryonal Tumor With Abundant Neuropil and True RosettesEpendymoblastomaMedulloepithelioma

Part of Cancer clinical trials.

This trial studies a drug called DFMO for children and young adults with certain rare cancers that have not responded to standard treatments or have come back. DFMO may help stop cancer cells from growing.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Ages
birth to 30 years
Study type
Expanded Access

Who can take part

  • You were diagnosed with a high-risk childhood cancer like neuroblastoma, medulloblastoma, or a rare tumor with certain genetic changes.
  • You are between 0 and 30 years old at the time of your first diagnosis.
  • You have finished standard treatments for your cancer.
  • You cannot join if you are currently taking another experimental drug.
  • If you could become pregnant, you must have a negative pregnancy test and agree to use effective birth control during and for 6 months after treatment.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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