Study of very rare inherited brain diseases over time
Part of Brain & nervous system, Cancer, Digestive system, Genetic & congenital, Hormones & metabolism clinical trials.
This study follows adults over time who have a very rare inherited brain disease, or whose illness seems like it may run in families. The goal is to better understand these conditions and how they progress.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be at least 18 years old
- You have a very rare inherited brain (neurologic) disease or symptoms
- Your condition is thought to be inherited in your family, or it’s still not diagnosed
- There are no stated study exclusions in the criteria provided
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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