ETX101 for children with SCN1A Dravet syndrome
Part of Brain & nervous system clinical trials.
This early-phase study tests how safe ETX101 is and whether it can help reduce seizures in young children with Dravet syndrome caused by an SCN1A gene change. It mainly enrolls infants and children with a specific type of seizure history and genetic result.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Your child’s age must fit the study’s age ranges (from at least 6 months up to under 18 years, depending on the part of the study)
- Genetic testing must show an SCN1A variant that is expected to reduce or stop gene function (predicted loss of function, likely or pathogenic)
- Your child’s first seizure must have started between 3 and 15 months of age
- Your child has a doctor diagnosis of Dravet syndrome, or the clinician strongly suspects it
- Your child is taking at least one seizure-prevention medicine every day
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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