Follow-up after half-matched bone marrow transplant for fanconi anemia
Treatments studied
Part of Genetic & congenital, Kidney & urinary, Women’s health & pregnancy clinical trials.
This study follows patients with Fanconi anemia who receive a bone marrow transplant from a half-matched donor. The goal is to monitor their health and outcomes after the transplant to learn more about how well this treatment works.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Diagnosis of Fanconi anemia confirmed by a chromosome test or genetic testing
- Age between 6 months and 60 years
- Severely low blood counts (for example, needing many transfusions or having very low platelets, white cells, or red cells)
- Signs of bone marrow problems, like a blood disorder or leukemia
- Access to a half-matched (haploidentical) donor who is not affected by Fanconi anemia
- Must have health insurance (French social security) and give consent (for minors, parent or guardian consent)
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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