Prenatal transplant for fetuses with Fanconi anemia
Part of Blood & lymphatic, Genetic & congenital, Hormones & metabolism clinical trials.
This trial tests giving a stem cell transplant to a fetus with Fanconi anemia before birth, using the mother's bone marrow cells. The goal is to help the baby's body make healthy blood cells before symptoms start.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Your pregnancy must be between 19 and 28 weeks at the time of the transplant.
- Your baby must have a confirmed diagnosis of Fanconi anemia from prenatal testing.
- You agree to an autopsy if the pregnancy does not continue.
- You must be healthy enough to donate bone marrow and undergo the procedure, with no conditions like severe obesity, heart disease, or active preterm labor.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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