New treatment for severe hemophilia a in children
Treatments studied
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This study tests a new treatment (FRSW107) for severe hemophilia A in children under 12. It aims to see if this treatment is safe and helps prevent bleeding episodes.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Male child under 12 years old
- Weighs more than 10 kg (about 22 lbs)
- Has severe hemophilia A with factor VIII level below 1%
- Has been previously treated with factor VIII for the required number of exposure days (more than 50 for under 6 years old, more than 150 for ages 6-12)
- Has normal blood clotting times (PT/INR) and no history of factor VIII inhibitors
- Has not had surgery or blood transfusions within the last 4 weeks
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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