Clin2
NCT06293729Possibly a fitNot yet recruiting

Gene therapy for inherited high cholesterol

Refractory HypercholesterolemiaFamilial Hypercholesterolemia

Part of Genetic & congenital, Hormones & metabolism clinical trials.

This trial tests a new gene therapy called NGGT006 for people with a genetic form of high cholesterol that doesn't improve with standard treatments. It aims to lower cholesterol levels and reduce the risk of heart problems.

Summary written for real people, not researchers, by Clin2.

Phase
Early Phase 1
Enrollment
9 people
Ages
18 years to 55 years
Study type
Interventional

Who can take part

  • You are between 18 and 55 years old.
  • You have a genetic form of high cholesterol confirmed by a blood test.
  • You have been on the highest dose of cholesterol-lowering medicines for at least 4 weeks, but your cholesterol is still high.
  • You have been following a healthy diet for at least 12 weeks and can keep it up during the trial.
  • You have not had a heart attack or stroke in the last 6 months.
  • You are willing to use effective birth control for at least a year after the treatment.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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