Study of inherited muscle diseases in children
Part of Bones, joints & muscles clinical trials.
This study looks at children with inherited muscle diseases (not Duchenne muscular dystrophy) to understand their symptoms and muscle function better. It may help doctors identify what type of muscle disease a child has and how it affects them day-to-day.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are between 2 and 18 years old
- You have been diagnosed with a genetic muscle disease that is not Duchenne muscular dystrophy (DMD)
- You and your parents agree to take part in the research
- You do not have Duchenne muscular dystrophy
- You do not have other conditions like spinal muscular atrophy, congenital myasthenia gravis, or nerve damage
- You do not have muscle problems caused by other illnesses like Guillain-Barre syndrome, or by long-term intensive care or hormone issues
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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