Natural history study of Duchenne muscular dystrophy in young boys
Part of Bones, joints & muscles, Brain & nervous system, Genetic & congenital clinical trials.
This study follows boys with Duchenne muscular dystrophy over time to better understand how the condition changes and how standard treatments affect health and function. It does not appear to test a new medicine, but it may help doctors plan better future care and studies.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Be a boy and between 4 and 9 years old
- Have a body weight or BMI at or below the 95th percentile
- Have confirmed Duchenne muscular dystrophy from gene testing
- Be able to do specific movement and walking tests (or have acceptable results already)
- Be on corticosteroids or able to start them before the study screening
- Not have serious heart or breathing problems (for example, heart pumping too low or needing ventilator support)
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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