Testing LY-M003 injection for Wilson disease
Part of Brain & nervous system, Digestive system, Genetic & congenital, Hormones & metabolism clinical trials.
This study tests an injection called LY-M003 for people with Wilson disease who have already been treated with standard medicines. The goal is to see if it is safe and works for them.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have confirmed Wilson disease with a specific gene change (ATP7B gene).
- You have been on standard treatments like D-penicillamine or zinc for at least 6 months.
- You must avoid high-copper foods (like shellfish and nuts) for the study period.
- You agree to prevent pregnancy and not donate blood, organs, or tissues during the study.
- You do not have severe liver problems like cirrhosis with complications or a MELD score above 13.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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