Super transplant for severe beta-thalassemia
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This trial tests a special type of stem cell transplant (called a super transplant) for children with a severe form of beta-thalassemia. It may be an option if you cannot or choose not to have a standard stem cell transplant or gene therapy.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Diagnosed with severe beta-thalassemia
- Be between 7 and 10 years old
- Weigh less than 40 kilograms (about 88 pounds)
- Have a donor who is fully or partially HLA-matched (a type of tissue match) and approved as a donor
- Agree to receive the super transplant and sign a consent form
- Not currently taking part in another drug trial
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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