Super transplant for severe thalassemia in children
Part of Blood & lymphatic clinical trials.
This trial tests a new type of transplant (called 'super transplantation') for children with severe thalassemia. It aims to help those who cannot get a fully matched donor or have chosen not to have standard treatments.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Diagnosed with severe Mediterranean anemia (thalassemia major)
- Age 7–12 years old and weight under 40 kg
- You either don't have a matched donor, or you have chosen not to have a standard stem cell transplant or gene therapy
- You have a donor who is HLA mismatched (not fully matched) but passes medical checks
- You and your family agree to try this experimental transplant and sign a consent form
- You do not have a mental health condition that would prevent participation
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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