Testing a new medicine for Leigh syndrome
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This trial tests a new medicine called TTI-0102 for people with Leigh syndrome. The goal is to find the best dose that might help slow down the disease and improve daily life.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You or your child must be between 5 and 55 years old.
- A confirmed diagnosis of Leigh syndrome or a similar condition (Leigh-like disorder) that affects brain development or function.
- Able to take a liquid medicine by mouth every day.
- Good liver and blood health (doctors will check this with simple tests).
- Not currently taking taurine supplements, and willing to stop them for the study.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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