Study of tti-0102 for leigh syndrome
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This trial tests a new drug, TTI-0102, for people with Leigh syndrome spectrum. The goal is to see if it helps with symptoms and to find the right dose.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Age between 5 and 55 years
- Confirmed diagnosis of Leigh syndrome or Leigh-like disorder with developmental issues
- Able to swallow the study drug (a liquid)
- Acceptable liver and kidney function
- No recent serious infections or other major health problems
- Willing to use birth control during the study
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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