Vosoritide for growth in infants with hypochondroplasia
Treatments studied
Part of Bones, joints & muscles, Genetic & congenital clinical trials.
This study tests a daily injection called vosoritide to see if it helps children with hypochondroplasia grow taller. It is for babies and toddlers up to 35 months old who are shorter than average for their age.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Your child must be between birth and 35 months old when starting the study.
- A genetic test must confirm a diagnosis of hypochondroplasia (a change in the FGFR3 gene).
- Your child's height must be significantly shorter than average for their age and sex.
- Your child's weight must be at least 6.6 pounds (3 kg) on the first day of treatment.
- Your child cannot have any other condition that causes short stature, like achondroplasia or Down syndrome.
- Your child cannot have taken growth hormone or certain other medicines in the past 6 months.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
Similar studies
Other trials that look related to this one.
This study observes children with hypochondroplasia to learn more about the condition. It does not involve any treatment—just monitoring and data collection to help future research.
This study is for children with hypochondroplasia, a condition that causes short stature. It will look at how the condition changes over time and aims to better understand it, with the goal of finding new treatments.
this study is a long-term extension of the main study for the drug which from Bio? bi? whatever? in the name? by?...????
This study tests an oral medication called infigratinib in children with hypochondroplasia, a form of short stature. It aims to see if the drug can help improve growth and is for children who are still growing.
This study tests whether an investigational drug can help children with idiopathic short stature (short height with no known cause) grow taller. It may be an option for children who are very short for their age and have not responded well to standard growth hormone therapy.
This trial tests a medication called vosoritide to see if it can help children with unexplained short stature grow taller. It's for kids who are very short for their age but have normal growth hormone levels and no other known cause.
Hear when a new Hypochondroplasia trial opens
We’ll email you when one opens — at most once a week, no account needed, unsubscribe anytime.