Gene therapy trial for Bietti's crystalline dystrophy
Part of Eyes & vision clinical trials.
This trial tests an investigational gene therapy called ZVS101e for people with Bietti's crystalline dystrophy (BCD), a rare inherited eye disease. It aims to see if the treatment can help slow vision loss or improve vision.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be at least 18 years old
- You must have a confirmed diagnosis of Bietti's crystalline dystrophy (BCD)
- Genetic testing must show changes in the CYP4V2 gene
- Your vision in the study eye must be 20/80 (ETDRS 60 letters) or worse
- You must not have had gene therapy or stem cell therapy for BCD before
- You cannot be pregnant or nursing
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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