Extension study of an investigational drug for late-onset pompe disease
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study is a follow-up for people with late-onset Pompe disease who have already completed a previous study of the investigational drug S-606001. It aims to continue monitoring safety and how well the treatment works over time.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must have completed a previous study with the study drug S-606001 for Pompe disease.
- You must weigh at least 40 kilograms (about 88 pounds).
- You cannot be pregnant or breastfeeding.
- You cannot be planning to conceive a child during the study.
- You cannot be enrolled in any other clinical trial or research study.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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