Testing treatments for progeria using lab-made stem cells
Part of Genetic & congenital, Hormones & metabolism clinical trials.
This study takes a small blood sample from people with progeria and turns the blood cells into stem cells in the lab. These stem cells are then used to test potential medicines, which could help find better treatments for progeria.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Diagnosed with Hutchinson-Gilford Progeria Syndrome (progeria)
- Currently an outpatient at the study hospital
- Age 19 or younger
- Able to provide a blood sample (or have a guardian consent)
- Safe to have blood drawn — no severe anemia, infection, or bleeding issues
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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