Register pregnant people with Pompe disease for pregnancy data
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study keeps a special record of pregnancies in people with Pompe disease to learn more about pregnancy outcomes and newborn information. It does not test a drug by itself—it collects health information to improve future care.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must already be enrolled in the Pompe registry (NCT00231400)
- You are currently pregnant or have been pregnant in the past
- You must have proof/medical records showing the pregnancy details
- You must sign consent forms before any study data is collected
- If you’ve had more than one pregnancy, the study encourages enrolling for each pregnancy
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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