Clin2
NCT04278131Possibly a fitRecruiting

Test eye gene therapy for retinitis pigmentosa

Retinitis Pigmentosa

Part of Eyes & vision, Genetic & congenital clinical trials.

This Phase 1/2 study tests a gene therapy treatment (BS01) in people with retinitis pigmentosa to try to improve or preserve vision. You may be a candidate if your vision in at least one eye is quite limited and you haven’t had certain gene therapies before.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 1/Phase 2
Enrollment
20 people
Ages
18 years and older
Study type
Interventional

Who can take part

  • You have a confirmed diagnosis of retinitis pigmentosa
  • One eye’s vision is at or below 20/160, or your field of vision is 30° or less
  • You have not previously received any AAV gene therapy in the past
  • You do not have large-amplitude nystagmus (big, noticeable eye shaking)

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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