Correcting a missing immune enzyme using an mRNA cell therapy
Part of Blood & lymphatic, Genetic & congenital, Immune system & allergy, Infections clinical trials.
This early-phase trial tests whether an mRNA-based treatment can correct a key immune problem in people with chronic granulomatous disease (CGD). It may help your immune cells work better against infections, but this is mainly to check safety and early signs of benefit.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are a male age 18 to 75
- Your CGD diagnosis is confirmed by specific lab tests (blood protein testing and/or genetic testing)
- You have a doctor you can contact at home for follow-up visits
- You can understand the study and sign consent
- You agree to use contraception if pregnancy is possible from your sex during screening through 3 months after infusion
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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