International registry for people with Wilson’s disease
Part of Brain & nervous system, Digestive system, Genetic & congenital, Hormones & metabolism clinical trials.
This trial is a patient registry that collects health information from people with Wilson’s disease, including those without symptoms yet and those taking any type of treatment. It helps researchers understand the disease and how it progresses, which can support future studies and care improvements.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You (or your legally approved guardian) can give consent to join the study in writing.
- Your study data use and privacy permissions must be completed as required in your country (for example, special consent forms for the US or EU sites).
- You have been diagnosed with Wilson’s disease, even if you have no symptoms yet.
- You can be on any treatment (prescription, traditional, homeopathic) or not on treatment at all.
- You must not refuse consent; if consent is refused, you cannot join.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
Similar studies
Other trials that look related to this one.
This study follows people who have the genetic cause of Wilson disease, including people who feel well and family members. Researchers want to better understand Wilson disease and what to watch for over time.
This study looks at the daily challenges people with Wilson's disease face in Upper Egypt, including emotional stress, diet, and access to services. If you join, you'll help researchers understand these issues so they can improve care for others like you.
This trial tests an experimental mRNA treatment (DSL101) for adults with Wilson disease. It's for people whose condition is stable on current therapy and who have certain genetic markers. The goal is to see if the new treatment can help the body process copper better and reduce the need for standard medicines.
This study tests a new gene therapy called LY-M003 that may help people with Wilson's disease by fixing the faulty gene that causes copper buildup. It's for adults who are already on standard treatment and have a confirmed genetic diagnosis.
This trial is testing an experimental gene therapy called PM577 that aims to fix the faulty gene causing Wilson disease. It might offer a new treatment option that could reduce or replace the need for daily medications.
This study looks for early signs of heart problems in people with Wilson's disease. It uses heart imaging tests to detect issues before symptoms appear, which could lead to earlier treatment and better heart health.
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