Clin2
NCT05754450Possibly a fitRecruiting

Extension study for AVTX-803 in LAD type II

Leukocyte Adhesion Deficiency

Part of Genetic & congenital, Immune system & allergy clinical trials.

This trial is a follow-up study testing whether AVTX-803 continues to be safe and effective for people with Leukocyte Adhesion Deficiency type II (LAD II). If you already took part in an earlier AVTX-803 LAD II study, this may be the next step while researchers monitor benefits and side effects.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 3
Enrollment
2 people
Ages
6 months to 75 years
Study type
Interventional

Who can take part

  • You finished the earlier AVTX-803 LAD-301 study
  • Your LAD II diagnosis has been confirmed by blood tests and genetic testing
  • Your hemoglobin level is not severely low (must be 8.0 g/dL or higher)
  • Your kidneys are working well enough (eGFR must be 90 mL/min or higher)
  • You have not had a bad reaction or allergy to fucose or ingredients in the medicine
  • You do not have a past history (in the investigator’s view) of not responding to fucose at adequate doses

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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