Clin2
NCT06374719Worth exploringRecruiting

TNNT1 myopathy natural history study

TNNT1-associated MyopathyInfantile-onset Nemaline Rod MyopathyMyopathies, NemalineMyopathyMyopathy, RodMyopathy; HereditaryAmish Nemaline MyopathyNemaline Myopathy 5

Part of Bones, joints & muscles, Brain & nervous system clinical trials.

This study follows people with a rare genetic muscle condition called TNNT1 myopathy over time. Researchers will track how the disease progresses to better understand it and help plan future treatments.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
40 people
Ages
Any age
Study type
Observational

Who can take part

  • You must have been diagnosed with a change in both copies of the TNNT1 gene (the gene linked to this condition).
  • Muscle weakness must have started in infancy or early childhood.
  • You cannot have any other medical condition that could affect the course of the disease or interfere with study procedures.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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