Study of GMP powder for PKU and tyrosinemia
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This trial tests a new powdered protein substitute (GMP) for people with PKU or tyrosinemia. It aims to see if it is a safe and effective option to help manage their condition.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are 3 years old or older
- You have PKU (any type) or tyrosinemia
- You have been taking at least one protein substitute providing at least 15g protein equivalents for at least 1 month
- You have a prescribed daily allowance of phenylalanine (or phenylalanine and tyrosine for TYR)
- You can take at least one sachet of the study product per day
- You are not pregnant or breastfeeding
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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