Clin2
NCT07063030Possibly a fitRecruiting

Gene therapy trial for AIPL1-related eye disease

Retinal Dystrophy

Part of Eyes & vision clinical trials.

This trial tests a gene therapy called LX107 for people with vision loss caused by changes in the AIPL1 gene. It aims to see if the treatment is safe and can improve vision.

Summary written for real people, not researchers, by Clin2.

Phase
Early Phase 1
Enrollment
13 people
Ages
4 years and older
Study type
Interventional

Who can take part

  • You or your child must be at least 4 years old.
  • You must have a confirmed diagnosis of AIPL1-related retinal disease with two changes in the AIPL1 gene.
  • Vision in the eye to be treated must be no better than approximately 20/70 on an eye chart.
  • You cannot have had certain eye surgeries in the past 6 months or other serious eye diseases.
  • You cannot have uncontrolled high blood pressure, poorly controlled diabetes, or certain infections or cancers.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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