A study of NTI164 for Rett syndrome in girls and young women
Part of Brain & nervous system, Genetic & congenital, Mental health clinical trials.
This trial tests a new study drug called NTI164 to see if it can safely help manage Rett syndrome symptoms in girls and young women. It is for those with classic Rett syndrome who have been stable recently and are not using certain other treatments.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are female and between 4 and 25 years old
- You weigh at least 12 kg (about 26 pounds)
- You have classic Rett syndrome confirmed by a MECP2 gene change
- Your Rett symptoms have been stable for the last 6 months
- Seizures are either absent or stable, and you have no serious heart, liver, or other major health problems
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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