Fenfluramine for Rett syndrome symptoms
Part of Brain & nervous system, Genetic & congenital clinical trials.
This study tests whether fenfluramine, a medication already used for seizures, can help people with Rett syndrome. It aims to see if it improves daily life and reduces symptoms.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have a confirmed diagnosis of typical or classic Rett syndrome with a MECP2 gene mutation.
- You are between 5 and 35 years old.
- Your symptoms have been stable for at least 6 months (no recent loss of walking, hand use, or communication).
- You have a caregiver who is 18 or older and can help with the study.
- You are not taking more than 4 seizure medications at the same time.
- You do not have serious heart or lung problems, or a history of cancer in the last 5 years.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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