Lamivudine Treatment Study for Rett Syndrome
Treatments studied
Part of Brain & nervous system, Genetic & congenital clinical trials.
This study tests whether lamivudine, a medication originally used for HIV, might help improve symptoms in people with Rett syndrome. Researchers will monitor how safe and effective the treatment is over time.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Confirmed diagnosis of Rett syndrome (clinical and genetic testing)
- Age 2 years or older
- Able to swallow liquid medication
- Generally stable health condition
- Parent or guardian able to provide consent and attend study visits
- Willing to have blood tests and possibly a small skin sample taken
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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