Family experiences with feeding and communication in SMA type 1
Part of Brain & nervous system, Digestive system, Ear, nose & throat, Genetic & congenital clinical trials.
This study interviews parents and families to understand their experiences with feeding and communication for children with SMA type 1. It aims to improve support and care for families.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Be a parent or legal guardian of a child with spinal muscular atrophy (SMA) type 1.
- Your child must have had treatment such as Spinraza, Zolgensma, or Evrysdi.
- You must be able to do an interview in English (no interpreter needed).
- You must not be a foster carer or a corporate parent (like a local authority).
- Grandparents or relatives with full parental responsibility can also take part.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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