Prednisolone for young boys with Duchenne muscular dystrophy
Part of Bones, joints & muscles, Brain & nervous system, Genetic & congenital clinical trials.
This trial compares two ways of taking the steroid prednisolone (every day vs every other day) in young boys with Duchenne muscular dystrophy. It aims to see if one schedule is better at maintaining muscle strength and function.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Be male
- Be between 4 and 10 years old
- Have a confirmed diagnosis of Duchenne muscular dystrophy (DMD) through genetic testing and high creatine kinase (CK) levels (above 1000 U/L)
- Be able to walk (not confined to a wheelchair)
- Not have heart or lung failure
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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