Treatment
Tofersen clinical trials
We’re tracking 2 recruiting studies that include Tofersen, each written for real people, not researchers, below.
Recruiting studies
- NCT07259980Recruiting
Long-term safety of tofersen for SOD-1 ALS
This study checks the long-term safety of the drug tofersen (also known as Qalsody) for people with a specific genetic type of ALS caused by SOD1 mutations. It aims to make sure the drug is safe over time by watching participants from registry networks.
Boston, MassachusettsAges 18 years+ - NCT07294144RecruitingPhase 2
Tofersen for ALS without SOD1 or FUS mutations
This trial tests if tofersen, a drug that targets a protein linked to ALS, can help people who have ALS but do not have mutations in the SOD1 or FUS genes. It aims to slow disease progression in those diagnosed within the last 2 years.
Atlanta, GeorgiaAges 18 years+
What Tofersen is being studied for
Conditions with recruiting Tofersen studies.
Common questions
- Are there clinical trials studying Tofersen?
- Yes. Clin2 currently lists 2 recruiting studies that include Tofersen, drawn from the U.S. registry and rewritten for real people so you can see what each is testing and who it's for.
- How do I know if I qualify for a Tofersen trial?
- Each study lists its own eligibility criteria — rules about condition, age, and prior treatments. On every Clin2 trial page we explain these in plain language and offer a short, optional pre-screen for a fit read. The study team makes the final decision.
- Is Tofersen an approved treatment?
- A drug being studied in a trial may be investigational (still being tested) or already approved and being studied for a new use. Each study page explains what phase it's in. Clin2 does not provide medical advice — talk with your doctor about whether Tofersen or a specific trial is right for you.
Related treatments
Clin2 helps you find and understand clinical trials and does not provide medical advice. Study data comes from ClinicalTrials.gov. A drug appearing here is being studied in a trial and may be investigational. Talk with your doctor about whether a specific treatment or trial is right for you.