Long-term safety of tofersen for SOD-1 ALS
Treatments studied
Part of Brain & nervous system, Hormones & metabolism clinical trials.
This study checks the long-term safety of the drug tofersen (also known as Qalsody) for people with a specific genetic type of ALS caused by SOD1 mutations. It aims to make sure the drug is safe over time by watching participants from registry networks.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must have been diagnosed with ALS
- You must have a confirmed SOD1 gene mutation
- You must be part of a registry network that shares medical information for ALS research
- You cannot be in another clinical trial testing tofersen or any other experimental drug at the same time
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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