Clin2
NCT02392572Possibly a fitTerminated

ONC201 for difficult blood cancers that are back or not responding

Recurrent Acute Lymphoblastic LeukemiaRecurrent Acute Myeloid LeukemiaRecurrent Myelodysplastic SyndromeRefractory Acute Lymphoblastic LeukemiaRefractory Acute Myeloid LeukemiaRefractory Myelodysplastic Syndrome

Treatments studied

Part of Blood & lymphatic, Cancer, Immune system & allergy clinical trials.

This trial tests ONC201, a study medicine, in adults with acute leukemia that has come back or did not respond, or high-risk myelodysplastic syndrome (MDS) that has limited treatment options. It may help shrink or control the cancer and support longer-lasting remission.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 1/Phase 2
Enrollment
58 people
Ages
18 years and older
Study type
Interventional

Who can take part

  • You are age 18 or older and have relapsed or refractory acute leukemia or high-risk MDS
  • You must be well enough to do daily activities (ECOG performance status 0–2)
  • If you can become pregnant, you must use reliable birth control and have a negative pregnancy test before starting; nursing is not allowed
  • Your last cancer treatments must be stopped long enough before starting (at least 2 weeks for chemo-like drugs, or 5 half-lives for others)
  • Your organ tests must be acceptable (kidney, liver blood tests) and you must not have significant unresolved side effects from prior treatment
  • You must not have certain serious uncontrolled health problems (like uncontrolled infection or unstable heart/psychiatric issues)

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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