Clin2
NCT04943198Possibly a fitRecruiting

Vemurafenib for hard-to-treat BRAF-mutant juvenile histiocytosis

Histiocytosis

Treatments studied

Part of Blood & lymphatic, Lungs & breathing clinical trials.

This Phase 2 study tests the medicine vemurafenib in children with refractory juvenile histiocytosis that has a BRAF mutation. It aims to find a better schedule (timing and dose) for treatment when standard therapies haven’t worked or the disease has come back.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 2
Enrollment
25 people
Ages
1 year to 18 years
Study type
Interventional

Who can take part

  • Your tumor tissue and/or blood test (circulating tumor DNA) shows a BRAF gene mutation
  • Your disease has not responded to standard treatment or has come back after treatment, including specific prior-treatment situations
  • You can join the related HISTIOGEN study and sign consent for this trial too
  • If you can get pregnant or cause pregnancy, you must use effective birth control during treatment and for at least 1 year after stopping
  • You cannot be pregnant or breastfeeding at enrollment
  • You must not have certain eye problems (like inflammation of the eye or blocked retinal veins) and must not have known allergy to vemurafenib

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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